Correction of Hunter syndrome in the MPSII mouse model by AAV2/8-mediated gene delivery

Author： Cardone Monica   Polito Vinicia Assunta   Pepe Stefano   Mann Linda   D'Azzo Alessandra   Auricchio Alberto   Ballabio Andrea   Cosma Maria Pia  

Publisher： Oxford University Press

ISSN： 1460-2083

Source： Human Molecular Genetics, Vol.15, Iss.7, 2006-04, pp. : 1225-1236

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