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Oxford University Press

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Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1 : effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors

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Gene therapy for retinitis pigmentosa and Leber congenital amaurosis caused by defects in AIPL1 : effective rescue of mouse models of partial and complete Aipl1 deficiency using AAV2/2 and AAV2/8 vectors

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