Arginine-rich cell-penetrating peptide dramatically enhances AMO-mediated ATM aberrant splicing correction and enables delivery to brain and cerebellum

Author： Du Liutao   Kayali Refik   Bertoni Carmen   Fike Francesca   Hu Hailiang   Iversen Patrick L.   Gatti Richard A.  

Publisher： Oxford University Press

ISSN： 1460-2083

Source： Human Molecular Genetics, Vol.20, Iss.16, 2011-08, pp. : 3151-3160

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