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Oxford University Press

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Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

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Therapeutic antisense-induced exon skipping in cultured muscle cells from six different DMD patients

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Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle

By Gebski B.L.   Mann C.J.   Fletcher S.   Wilton S.D.  

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2′-O-Methyl RNA/Ethylene-Bridged Nucleic Acid Chimera Antisense Oligonucleotides to Induce Dystrophin Exon 45 Skipping

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Genes, Vol. 8, Iss. 2, 2017-02 ,pp. : 67-67

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