SAHA ameliorates the SMA phenotype in two mouse models for spinal muscular atrophy

By Riessland Markus   Ackermann Bastian   Frster Anja   Jakubik Miriam   Hauke Jan   Garbes Lutz   Fritzsche Ina   Mende Ylva   Blumcke Ingmar   Hahnen Eric   Wirth Brunhilde  

Human Molecular Genetics, Vol. 19, Iss. 8, 2010-04 ,pp. : 1492-1506

Oxford University Press

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Cardiac defects contribute to the pathology of spinal muscular atrophy models

By Shababi Monir   Habibi Javad   Yang Hsiao T.   Vale Spencer M.   Sewell Will A.   Lorson Christian L.  

Human Molecular Genetics, Vol. 19, Iss. 20, 2010-10 ,pp. : 4059-4071

Oxford University Press

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Delivery of a read-through inducing compound, TC007, lessens the severity of a spinal muscular atrophy animal model

By Mattis Virginia B.   Ebert Allison D.   Fosso Marina Y.   Chang Cheng-Wei   Lorson Christian L.  

Human Molecular Genetics, Vol. 18, Iss. 20, 2009-10 ,pp. : 3906-3913

Oxford University Press

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Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy

By Baughan Travis D.   Dickson Alexa   Osman Erkan Y.   Lorson Christian L.  

Human Molecular Genetics, Vol. 18, Iss. 9, 2009-05 ,pp. : 1600-1611

Oxford University Press

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Selective vulnerability of motor neurons and dissociation of pre- and post-synaptic pathology at the neuromuscular junction in mouse models of spinal muscular atrophy

By Murray Lyndsay M.   Comley Laura H.   Thomson Derek   Parkinson Nick   Talbot Kevin   Gillingwater Thomas H.  

Human Molecular Genetics, Vol. 17, Iss. 7, 2008-04 ,pp. : 949-962

Oxford University Press

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