Intrathecal Enzyme Replacement Therapy for Mucopolysaccharidosis I: Translating Success in Animal Models to Patients

Publisher： Bentham Science Publishers

E-ISSN： 1873-4316|12|6|946-955

ISSN： 1389-2010

Source： Current Pharmaceutical Biotechnology, Vol.12, Iss.6, 2011-06, pp. : 946-955

Disclaimer: Any content in publications that violate the sovereignty, the constitution or regulations of the PRC is not accepted or approved by CNPIEC.

Previous Menu Next

Abstract

Related content

The first 5years of clinical experience with laronidase enzyme replacement therapy for mucopolysaccharidosis I

By Wraith J E  

Expert Opinion on Pharmacotherapy, Vol. 6, Iss. 3, 2005-03 ,pp. : 489-506

Informa Healthcare

Access to resources Recommend Favorite

Development of nanoparticle-bound arylsulfatase B for enzyme replacement therapy of mucopolysaccharidosis VI

By Mühlstein A.   Gelperina S.   Kreuter J.  

Die Pharmazie - An International Journal of Pharmaceutical Sciences, Vol. 68, Iss. 7, 2013-07 ,pp. : 549-554

Govi-Verlag

Access to resources Recommend Favorite

Enzyme Replacement Therapy in Patients with Fabry's Disease

By Tsuboi K  

The Journal of International Medical Research, Vol. 35, Iss. 4, 2007-07 ,pp. : 574-581

Field House Publishing

Access to resources Recommend Favorite

-L-iduronidase shows long-term efficacy in the treatment of patients with mucopolysaccharidosis I

By  

Inpharma, Vol. 1, Iss. 1289, 2001-01 ,pp. : 14-14

Adis International

Access to resources Recommend Favorite

Chloramphenicol Enhances IDUA Activity on Fibroblasts from Mucopolysaccharidosis I Patients

By  

Current Pharmaceutical Biotechnology, Vol. 14, Iss. 2, 2013-02 ,pp. : 194-198

Bentham Science Publishers

Access to resources Recommend Favorite