Chapter
PCSK9 & Familial Hypercholesterolemia
Hereditary Tyrosinemia Type I (HT-I)
Concerns in the Cas9 Delivery Systems
Applications and Advances of CRISPR/Cas9, a Versatile Tool for Genome Editing in Animal Models
A List of Non-Standard Abbreviations
CRISPR and CRISPR/Cas9 System
Applications of CRISPR Technology on Animal Model Generation
Conclusion and Perspective
Gene Targeting on Cyp2c Locus in Rats Using the CRISPR/Cas9 System
A List of Non-Standard Abbreviations
Cyp2c6, Cyp2c11 and Cyp2c12 KO Target Site Selection
DNA Constructs and In Vitro Transcription
Co-Microinjection of sgRNA and Cas9 mRNA into Zygotes
Genotyping of Founders and Progenies
Cyp2c6, Cyp2c11 and Cyp2c12 KO Target Site Selection
Genotyping of F0 Founders
Applications of CRISPR/Cas9 for Therapy in Human Genetic Diseases
Applications of CRISPR/Cas9 Genome Editing in Diseases
CRISPR/Cas9 Gene-Editing in Point Mutation-Induced Diseases
CRISPR/Cas9 Gene-Editing in Gene or Genome Deletion-Related Diseases
CRISPR/Cas9 Gene-Editing in Chromosomal Inversion- Related Diseases
Utilization of CRISPR in Gene Function and Drug Target Validation
Characteristics of CRISPR/Cas9 System
Different CRISPR/Cas9 Systems
Applications of CRISPR/Cas
Drug Target Identification
Drug Resistance-Associated Gene Identification
Applications of CRISPR/Cas9 in Plant Genome Editing
Cases About CRISPR/Cas9 in Plant Gene Editing
Medicinal Plant Gene Function Study
The Generation of New Better Crop Varieties
The Difficulties Needed to Be Overcome in Plant Genome Editing
Genome Editing on Human Embryos by CRISPR is Attractive but Controversial
Gene Editing on Embryos Using CRISPR