Gene Therapy for Pyruvate Dehydrogenase E1 Deficiency Using Recombinant Adeno-Associated Virus 2 (rAAV2) Vectors

By Owen R.   Mandel R.J.   Ammini C.V.   Conlon T.J.   Kerr D.S.   Stacpoole P.W.   Flotte T.R.  

Molecular Therapy, Vol. 6, Iss. 3, 2002-09 ,pp. : 394-399

Elsevier

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Self-complementary adeno-associated virus serotype 2 vector: global distribution and broad dispersion of AAV-mediated transgene expression in mouse brain

By Fu H.   Muenzer J.   Samulski R.J.   Breese G.   Sifford J.   Zeng X.   McCarty D.M.  

Molecular Therapy, Vol. 8, Iss. 6, 2003-12 ,pp. : 911-917

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Successful transgene expression with serial doses of aerosolized rAAV2 vectors in rhesus macaques

By Fischer A.C.   Beck S.E.   Smith C.I.   Laube B.L.   Askin F.B.   Guggino S.E.   Adams R.J.   Flotte T.R.   Guggino W.B.  

Molecular Therapy, Vol. 8, Iss. 6, 2003-12 ,pp. : 918-926

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Persistent phenotypic correction of central diabetes insipidus using adeno-associated virus vector expressing Arginine-Vasopressin in brattleboro rats

By Ideno J.   Mizukami H.   Honda K.   Okada T.   Hanazono Y.   Kume A.   Saito T.   Ishibashi S.   Ozawa K.  

Molecular Therapy, Vol. 8, Iss. 6, 2003-12 ,pp. : 895-902

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Adeno-associated virus-mediated gene transfer of a secreted decoy human macrophage scavenger receptor reduces atherosclerotic lesion formation in LDL receptor knockout mice

By Jalkanen J.   Leppanen P.   Pajusola K.   Narvanen O.   Mahonen A.   Vahakangas E.   Greaves D.R.   Bueler H.   Yla-Herttuala S.  

Molecular Therapy, Vol. 8, Iss. 6, 2003-12 ,pp. : 903-910

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