Gene therapy using self-complementary Y733F capsid mutant AAV2/8 restores vision in a model of early onset Leber congenital amaurosis

Author： Ku Cristy A.   Chiodo Vince A.   Boye Sanford L.   Goldberg Andrew F.X.   Li Tiansen   Hauswirth William W.   Ramamurthy Visvanathan  

Publisher： Oxford University Press

ISSN： 1460-2083

Source： Human Molecular Genetics, Vol.20, Iss.23, 2011-12, pp. : 4569-4581

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