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Oxford University Press

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A novel function for the survival motoneuron protein as a translational regulator

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Oxford University Press

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Protective effects of cardiotrophin-1 adenoviral gene transfer on neuromuscular degeneration in transgenic ALS mice

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Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy

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Molecular dissection of ALS-associated toxicity of SOD1 in transgenic mice using an exon-fusion approach

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