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Notch Signaling Pathway Is Activated in Motoneurons of Spinal Muscular Atrophy

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Investigation of New Morpholino Oligomers to Increase Survival Motor Neuron Protein Levels in Spinal Muscular Atrophy

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A Perturbed MicroRNA Expression Pattern Characterizes Embryonic Neural Stem Cells Derived from a Severe Mouse Model of Spinal Muscular Atrophy (SMA)

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Galectins as Molecular Targets for Therapeutic Intervention

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