Using CRISPR/Cas9-Mediated GLA Gene Knockout as an In Vitro Drug Screening Model for Fabry Disease

By Song Hui-Yung   Chiang Huai-Chih   Tseng Wei-Lien   Wu Ping   Chien Chian-Shiu   Leu Hsin-Bang   Yang Yi-Ping   Wang Mong-Lien   Jong Yuh-Jyh   Chen Chung-Hsuan   Yu Wen-Chung   Chiou Shih-Hwa  

International Journal of Molecular Sciences, Vol. 17, Iss. 12, 2016-12 ,pp. : 2089-2089

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CRISPR-Cas9 Mediated Gene-Silencing of the Mutant Huntingtin Gene in an In Vitro Model of Huntington’s Disease

By Kolli Nivya   Lu Ming   Maiti Panchanan   Rossignol Julien   Dunbar Gary L.  

International Journal of Molecular Sciences, Vol. 18, Iss. 4, 2017-04 ,pp. : 754-754

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CRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient Cells

By Skvarova Kramarzova Karolina   Osborn Mark J.   Webber Beau R.   DeFeo Anthony P.   McElroy Amber N.   Kim Chong Jai   Tolar Jakub  

International Journal of Molecular Sciences, Vol. 18, Iss. 6, 2017-06 ,pp. : 1269-1269

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Biased and Unbiased Methods for the Detection of Off-Target Cleavage by CRISPR/Cas9: An Overview

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International Journal of Molecular Sciences, Vol. 17, Iss. 9, 2016-09 ,pp. : 1507-1507

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CRISPR/Cas9-Mediated Rapid Generation of Multiple Mouse Lines Identified Ccdc63 as Essential for Spermiogenesis

By Young Samantha A. M.   Miyata Haruhiko   Satouh Yuhkoh   Kato Hirotaka   Nozawa Kaori   Isotani Ayako   Aitken R. John   Baker Mark A.   Ikawa Masahito  

International Journal of Molecular Sciences, Vol. 16, Iss. 10, 2015-10 ,pp. : 24732-24750

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