A Roadmap to Newborn Screening for Duchenne Muscular Dystrophy

By Al-Zaidy Samiah A.   Lloyd-Puryear Michele   Kennedy Annie   Lopez Veronica   Mendell Jerry R.  

International Journal of Neonatal Screening, Vol. 3, Iss. 2, 2017-04 ,pp. : 8-8

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Serum Levels of MicroRNA-206 and Novel Mini-STR Assays for Carrier Detection in Duchenne Muscular Dystrophy

By Anaya-Segura Mónica Alejandra   Rangel-Villalobos Héctor   Martínez-Cortés Gabriela   Gómez-Díaz Benjamín   Coral-Vázquez Ramón Mauricio   Zamora-González Edgar Oswaldo   García Silvia   López-Hernández Luz Berenice  

International Journal of Molecular Sciences, Vol. 17, Iss. 8, 2016-08 ,pp. : 1334-1334

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Current Challenges and Future Directions in Recombinant AAV-Mediated Gene Therapy of Duchenne Muscular Dystrophy

By Okada Takashi   Takeda Shin'ichi  

Pharmaceuticals, Vol. 6, Iss. 7, 2013-06 ,pp. : 813-836

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Duchenne Muscular Dystrophy Newborn Screening, a Case Study for Examining Ethical and Legal Issues for Pilots for Emerging Disorders: Considerations and Recommendations

By Lloyd-Puryear Michele A.   Crawford Thomas O.   Brower Amy   Stephenson Kristin   Trotter Tracy   Goldman Edward   Goldenberg Aaron   Howell R. Rodney   Kennedy Annie   Watson Michael  

International Journal of Neonatal Screening, Vol. 4, Iss. 1, 2018-01 ,pp. : 6-6

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Modulation of Protein Quality Control and Proteasome to Autophagy Switch in Immortalized Myoblasts from Duchenne Muscular Dystrophy Patients

By Wattin Marion   Gaweda Loïc   Muller Pascale   Baritaud Mathieu   Scholtes Charlotte   Lozano Chloé   Gieseler Kathrin   Kretz-Remy Carole  

International Journal of Molecular Sciences, Vol. 19, Iss. 1, 2018-01 ,pp. : 178-178

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