Antisense-induced exon skipping restores dystrophin expression in DMD patient derived muscle cells

By Baas F.   van Deutekom J.C.T.   Bremmer-Bout M.   Janson A.A.M.   Ginjaar I.B.   Dunnen J.T.d.   van Ommen G-J.B.  

Human Molecular Genetics, Vol. 10, Iss. 15, 2001-07 ,pp. : 1547-1554

Oxford University Press

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Morpholino antisense oligonucleotide induced dystrophin exon 23 skipping in mdx mouse muscle

By Gebski B.L.   Mann C.J.   Fletcher S.   Wilton S.D.  

Human Molecular Genetics, Vol. 12, Iss. 15, 2003-08 ,pp. : 1801-1811

Oxford University Press

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Rescue of severely affected dystrophin/utrophin-deficient mice through scAAV-U7snRNA-mediated exon skipping

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Human Molecular Genetics, Vol. 21, Iss. 11, 2012-06 ,pp. : 2559-2571

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Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping

By Bertoni Carmen   Lau Catherine   Rando Thomas A.  

Human Molecular Genetics, Vol. 12, Iss. 10, 2003-05 ,pp. : 1087-1099

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A fusion peptide directs enhanced systemic dystrophin exon skipping and functional restoration in dystrophin-deficient mdx mice

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Human Molecular Genetics, Vol. 18, Iss. 22, 2009-11 ,pp. : 4405-4414

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