Improvement of life quality measured by Lansky Score after enzymatic replacement therapy in children with Gaucher disease type 1

Publisher： John Wiley & Sons Inc

E-ISSN： 2324-9269|6|1|27-34

ISSN： 2324-9269

Source： Molecular Genetics & Genomic Medicine, Vol.6, Iss.1, 2018-01, pp. : 27-34

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