Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/ mdx mice

By Wells D.J.   Fabb S.A.   Serpente P.   Dickson G.  

Human Molecular Genetics, Vol. 11, Iss. 7, 2002-04 ,pp. : 733-741

Oxford University Press

Access to resources Recommend Favorite

Prolonged dystrophin expression and functional correction of mdx mouse muscle following gene transfer with a helper-dependent (gutted) adenovirus-encoding murine dystrophin

By Gilbert Rénald  

Human Molecular Genetics, Vol. 12, Iss. 11, 2003-06 ,pp. : 1287-1299

Oxford University Press

Access to resources Recommend Favorite

Preventing phosphorylation of dystroglycan ameliorates the dystrophic phenotype in mdx mouse

By Miller Gaynor   Moore Chris J.   Terry Rebecca   La Riviere Tracy   Mitchell Andrew   Piggott Robert   Dear T. Neil   Wells Dominic J.   Winder Steve J.  

Human Molecular Genetics, Vol. 21, Iss. 20, 2012-10 ,pp. : 4508-4520

Oxford University Press

Access to resources Recommend Favorite

Gene Transfer into the Mouse Retina Mediated by an Adeno-Associated Viral Vector

By Ali Robin R.   Reichel Martin B.   Thrasher Adrian J.   Levinsky Roland J.   Kinnon Christine   Kanuga Naheed   Hunt David M.   Bhattacharya Shomi S.  

Human Molecular Genetics, Vol. 5, Iss. 5, 1996-01 ,pp. : 591-594

Oxford University Press

Access to resources Recommend Favorite

Overexpression of a calpastatin transgene in mdx muscle reduces dystrophic pathology

By Spencer M.J.  

Human Molecular Genetics, Vol. 11, Iss. 21, 2002-10 ,pp. : 2645-2655

Oxford University Press

Access to resources Recommend Favorite