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Oxford University Press

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Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy

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Human Molecular Genetics, Vol. 15, Iss. 1, 2006-01 ,pp. : 53-64

Oxford University Press

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Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/ mdx mice

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Human Molecular Genetics, Vol. 11, Iss. 15, 2002-07 ,pp. : 1719-1730

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Viral Vector-Mediated Antisense Therapy for Genetic Diseases

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