Gene Transfer into the Mouse Retina Mediated by an Adeno-Associated Viral Vector

By Ali Robin R.   Reichel Martin B.   Thrasher Adrian J.   Levinsky Roland J.   Kinnon Christine   Kanuga Naheed   Hunt David M.   Bhattacharya Shomi S.  

Human Molecular Genetics, Vol. 5, Iss. 5, 1996-01 ,pp. : 591-594

Oxford University Press

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Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

By Lostal William   Bartoli Marc   Bourg Nathalie   Roudaut Carinne   Bentab Azeddine   Miyake Katsuya   Guerchet Nicolas   Fougerousse Franoise   McNeil Paul   Richard Isabelle  

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Oxford University Press

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Adeno-associated virus vector gene transfer and sarcolemmal expression of a 144 kDa micro-dystrophin effectively restores the dystrophin-associated protein complex and inhibits myofibre degeneration in nude/ mdx mice

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Human Molecular Genetics, Vol. 11, Iss. 7, 2002-04 ,pp. : 733-741

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Increased motoneuron survival and improved neuromuscular function in transgenic ALS mice after intraspinal injection of an adeno-associated virus encoding Bcl-2

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Human Molecular Genetics, Vol. 9, Iss. 5, 2000-03 ,pp. : 803-811

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Importance of the glycosylation and polyadenylation variants in metachromatic leukodystrophy pseudodeficiency phenotype

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Human Molecular Genetics, Vol. 7, Iss. 8, 1998-08 ,pp. : 1215-1219

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