Delivery of a read-through inducing compound, TC007, lessens the severity of a spinal muscular atrophy animal model

Author： Mattis Virginia B.   Ebert Allison D.   Fosso Marina Y.   Chang Cheng-Wei   Lorson Christian L.  

Publisher： Oxford University Press

ISSN： 1460-2083

Source： Human Molecular Genetics, Vol.18, Iss.20, 2009-10, pp. : 3906-3913

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