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Oxford University Press

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Transplacental injection of somite-derived cells in mdx mouse embryos for the correction of dystrophin deficiency

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Intracerebral adeno-associated virus-mediated gene transfer in rapidly progressive forms of metachromatic leukodystrophy

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A single postnatal injection of oxytocin rescues the lethal feeding behaviour in mouse newborns deficient for the imprinted Magel2 gene

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